Gripping story this morning about children suffering from MLD a brain decaying disease that typically kills children before the age of 6. The family who had one child die from the disease and two others diagnosed found a clinical trial in Italy, and the other two kids are fine. However, gene therapy is not available yet in the US. They had some child die during clinical trials, and never restarted it. Now, the trial is closed in Italy. Even though this condition is rare, people need resources. I wonder if petitioning NIH would help? I lost focus on the story but I know the parents of another affected child were raising money. Maybe they were trying to get a private company to do this.